May 22, 2013
11:00 am to 12:00 PM EDT

Sponsored by

Symposium Course Description:

This webinar will discuss the SMA-MAP, a multiplexed immunoassay biomarker panel for spinal muscular atrophy. Topics include the development and utility of SMA-MAP for classification of patients, and current efforts to validate the panel for tracking disease progression and drug response. We will also discuss the applicability of our schema for developing biomarkers in other rare, pediatric diseases.

Who Should Attend:

  • Biotech and pharma VPs
  • Directors
  • Scientists and academic Clinicians with roles in Biomarkers
  • Translational Medicine
  • Clinical Research
  • Biostatistics and rare disease drug development.

Program Agenda:

  • Introduction and SMA biomarker development 5min
  • SMA biomarker studies 5 min
  • Development and confirmation of SMA-MAP and the motor score prediction tool 10min
  • Ongoing research and applications 5 min
  • Questions 5 min.

Speaker Information:

Dione T. Kobayashi PhD
Translational Medicine Consultant to the SMA Foundatio